Initial Human Experience with SBC-102, a Recombinant Enzyme Replacement Therapy in Adults with Lysosomal Acid Lipase Deficiency 8th Annual World Symposium of the Lysosomal Disease Network Enns, G., Balwani, M., Deegan, P., Malinova, V. R., Honzik, H., Sharma, R., Valayannopoulos, V., Wraith, E., Schneider, E., Burg, J., Quinn, A. ACADEMIC PRESS INC ELSEVIER SCIENCE. 2012: S29–S29

View details for DOI 10.1016/j.ymgme.2011.11.055

View details for Web of Science ID 000299758300066