Results of a Global Phase 3, Randomized, Double-Blind, Placebo-Controlled Trial Evaluating the Efficacy and Safety of Sebelipase Alfa as an Enzyme Replacement Therapy in Children and Adults with Lysosomal Acid Lipase Deficiency Balwani, M., Burton, B., Baric, I., Bialer, M., Burrow, T. A., Camarena Grande, C., Coker, M., Consuelo Sanchez, A., Deegan, P., Di Rocco, M., Enns, G. M., Erbe, R. W., Ezgu, F., Feillet, F., Ficicioglu, C., Furuya, K. N., Bernardo Guelbert, N., Kane, J., Kostyleva, M., Laukaitis, C. M., Malinova, V., Mengel, E., Murphy, E., Neilan, E. G., Nightingale, S., Pastor Rosado, J., Peters, H., Rahman, Y., Scarpa, M., Schwab, K., Smolka, V., Taybert, J., Valayannopoulos, V., Wood, M., Zeniya, M., Yang, Y., Eckert, S., Rojas-Caro, S., Quinn, A. G. WILEY-BLACKWELL. 2014: 1270A

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