An Open-Label, Dose-Escalation Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics and Pharmacodynamics of Cysteamine Bitartrate Delayed-release Capsules (RP103) for Treatment of Children with Inherited Mitochondrial Disease (RP103-MITO-001) Cohen, B. H., Enns, G. M., Haas, R., Longo, N., Scaglia, F., Lang, W., Sile, S. ELSEVIER SCI LTD. 2016: 117

View details for Web of Science ID 000388431500086