Trial ID or NCT#



not recruiting iconNOT RECRUITING


The main objective of this study is to provide confirmatory evidence of efficacy of eteplirsen (AVI-4658) in Duchenne muscular dystrophy (DMD) patients that are amenable to skipping exon 51. Additional objectives include evaluation of safety and biomarkers. Sites are currently being initiated into the study. Initiation of approximately 39 planned sites in the United States is expected to be completed by January 2015. The initiated sites can be found in the "Contacts and Locations" section of this posting in addition to a listing of the city and states of sites the investigators are working to initiate. This information will be updated on a rolling basis as additional sites are initiated.


John W. Day, MD, PhD

Contact us to find out if this trial is right for you.


Shirley Paulose
(650) 724-3792