Trial ID or NCT#

NCT01721733

Status

RECRUITING

Purpose

The purpose of this study is to evaluate the effects of EPI-743 in children with Leigh syndrome on disease severity, neuromuscular function, respiratory function, disease morbidity and mortality and disease associated biomarkers.

Official Title

A Phase 2B Randomized, Placebo Controlled, Double Blind Clinical Trial of EPI-743 in Children With Leigh Syndrome

Eligibility Criteria

Ages Eligible for Study: 6 Years to 17 Years
Sexes Eligible for Study: All
Accepts Healthy Volunteers: No

Investigator(s)

Gregory Enns
Geneticist
Professor of Pediatrics (Genetics) at the Lucile Salter Packard Children's Hospital

Contact us to find out if this trial is right for you.

CONTACT

Gregory Enns, MD
(650) 498-5798