EPI-743 for Mitochondrial Respiratory Chain Diseases

Trial ID or NCT#

NCT01370447

Status

not recruiting iconNOT RECRUITING

Purpose

This study will evaluate the safety and efficacy of EPI-743 in participants with severe mitochondrial respiratory chain diseases who are considered to be within 90 days of end-of-life care.

Official Title

Emergency Use Protocol for EPI-743 in Acutely Ill Patients With Inherited Mitochondrial Respiratory Chain Disease Within 90 Days of End-of-Life Care

Eligibility Criteria

Ages Eligible for Study: Older than 1 Year
Sexes Eligible for Study: All
Accepts Healthy Volunteers: No

Investigator(s)

Gregory Enns

Contact us to find out if this trial is right for you.

Contact

Greg Enns, MD
(650) 498-5798