A Study of AG-348 in Adult Participants With Pyruvate Kinase (PK) Deficiency

Trial ID or NCT#

NCT02476916

Status

recruiting iconRECRUITING

Purpose

Study AG348-C-003 is a multicenter study designed to evaluate the safety and efficacy of different dose levels of AG-348 (mitapivat) in participants with PK deficiency.

Official Title

A Phase 2, Open Label, Randomized, Dose Ranging, Safety, Efficacy, Pharmacokinetic and Pharmacodynamic Study of AG-348 in Adult Patients With Pyruvate Kinase Deficiency

Eligibility Criteria

Ages Eligible for Study: Older than 18 Years
Sexes Eligible for Study: All
Accepts Healthy Volunteers: No

Investigator(s)

Bertil Glader
Anupama Narla

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Contact

Heather Hilmoe
650-725-1662