A Study of AG-348 in Adult Participants With Pyruvate Kinase (PK) Deficiency
Trial ID or NCT#
Status
Purpose
Study AG348-C-003 is a multicenter study designed to evaluate the safety and efficacy of different dose levels of AG-348 (mitapivat) in participants with PK deficiency.
Official Title
A Phase 2, Open Label, Randomized, Dose Ranging, Safety, Efficacy, Pharmacokinetic and Pharmacodynamic Study of AG-348 in Adult Patients With Pyruvate Kinase Deficiency
Eligibility Criteria
Investigator(s)
Contact us to find out if this trial is right for you.
Contact
Heather Hilmoe
650-725-1662
View on ClinicalTrials.gov