Trial ID or NCT#

NCT01370447

Status

NOT RECRUITING

Purpose

This study evaluates the safety and efficacy of EPI-743 in patients with severe mitochondrial respiratory chain diseases who are considered to be within 90 days of end-of-life care.

Official Title

Emergency Use Protocol for EPI-743 in Acutely Ill Patients With Inherited Mitochondrial Respiratory Chain Disease Within 90 Days of End-of-Life Care

Eligibility Criteria

Ages Eligible for Study: Older than 1 Year
Sexes Eligible for Study: All
Accepts Healthy Volunteers: No

Investigator(s)

Gregory Enns
Geneticist
Professor of Pediatrics (Genetics) at the Lucile Salter Packard Children's Hospital

Contact us to find out if this trial is right for you.

CONTACT

Greg Enns, MD
(650) 498-5798