Patient-Centered Therapy Development for Myotonic Dystrophy: Report of the Myotonic Dystrophy Foundation-Sponsored Workshop THERAPEUTIC INNOVATION & REGULATORY SCIENCE Hesterlee, S., Amur, S., Bain, L. J., Carulli, J., Clarke, S., Day, J. W., Gagnon, C., Hagerman, K., Heatwole, C., Johnson, N. E., Moxley, R., Patel, N., Thornton, C., Kessel, W., White, M. 2017; 51 (4): 516–22

View details for DOI 10.1177/2168479016683988

View details for Web of Science ID 000404999500017