Results of a phase 2 open-label study of ISIS-SMNRx in patients with infantile (Type 1) spinal muscular atrophy Finkel, R. S., Day, J., Chiriboga, C., Vasjar, J., Cook, D., Watson, K., Paulose, S., McMillian, L., Cruz, R., Montes, J., De Vivo, D. C., Yamashita, M., McGuire, D., Alexander, K., Norris, D., Bennett, C. F., Bishop, K. PERGAMON-ELSEVIER SCIENCE LTD. 2014: 920

View details for DOI 10.1016/j.nmd.2014.06.416

View details for Web of Science ID 000342870200413