JEWELFISH: safety and pharmacodynamic data in patients with spinal muscular atrophy (SMA) receiving treatment with risdiplam (RG7916) that have previously been treated with nusinersen Chiriboga, C., Mercuri, E., Fischer, D., Day, J., Kraus, D., Yeung, W., Kletzl, H., Gerber, M., Cleary, Y., Gorni, K. PERGAMON-ELSEVIER SCIENCE LTD. 2019: S187

View details for DOI 10.1016/j.nmd.2019.06.525

View details for Web of Science ID 000487768600511