The restore registry: A resource for measuring and improving spinal muscular atrophy outcomes Servais, L., Day, J. W., De Vivo, D. C., Kirschner, J., Mercuri, E., Muntoni, F., Shieh, P. B., Tizzano, E., Droege, M., Dabbous, O., Khan, F., Anderson, F. A., Finkel, R. S. ELSEVIER. 2019

View details for DOI 10.1016/j.jns.2019.10.330

View details for Web of Science ID 000516770701133