SUNFISH Part 2: Efficacy and safety of risdiplam (RG7916) in patients with Type 2 or non-ambulant Type 3 spinal muscular atrophy (SMA) Mercuri, E., Barisic, N., Boespflug-Tanguy, O., Day, J. W., Deconinck, N., Kostera-Pruszczyk, A., Masson, R., Mazzone, E., Nascimento, A., Saito, K., Vlodavets, D., Fuerst-Recktenwald, S., Fuhrer, S., Gerber, M., Gorni, K., Kletzl, H., Martin, C., Yeung, W. Y., Vuillerot, C. WILEY. 2020: 869

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