Long-term follow-up (LTFU) of onasemnogene abeparvovec gene therapy in spinal muscular atrophy (SMA) Mendell, J., Finkel, R., Mercuri, E., Strauss, K., Day, J., Kleyn, A., Chand, D., Tauscher-Wisniewski, S., Meriggioli, M. PERGAMON-ELSEVIER SCIENCE LTD. 2021: S132-S133

View details for DOI 10.1016/j.nmd.2021.07.298

View details for Web of Science ID 000697873700283