AT845 gene replacement therapy for late onset Pompe disease: An update on safety and preliminary efficacy data from FORTIS, a phase I/II open-label clinical study Manera, J., Mozaffar, T., Day, J. W., Longo, N., Straub, V., Varfaj, F., Chou, H., Maruoka, M., Han, C., Coats, J., Maziere, J. A., Walzer, M., Smith, A. R. ACADEMIC PRESS INC ELSEVIER SCIENCE. 2023: 34-35

View details for DOI 10.1016/j.ymgme.2022.107078

View details for Web of Science ID 001013039500096