Efficacy and safety of avalglucosidase alfa in participants with late-onset Pompe disease after 145 weeks of treatment during the COMET trial Kishnani, P. S., Diaz-Manera, J., Kushlaf, H., Ladha, S., Mozaffar, T., Straub, V., Toscano, A., van der Ploeg, A. T., Clemens, P. R., Day, J. W., Illarioshkin, S., Roberts, M. E., Attarian, S., Carvalho, G., Erdem-Ozdamar, S., Goker-Alpan, O., Kostera-Pruszczyk, A., Haack, K., Huynh-Ba, O., Tammireddy, S., Thibault, N., Zhou, T., Dimachkie, M. M., Schoser, B., COMET Investigator Grp ACADEMIC PRESS INC ELSEVIER SCIENCE. 2023: 74

View details for DOI 10.1016/j.ymgme.2022.107185

View details for Web of Science ID 001013039500203