Efficient CRISPR/Cas9-Mediated Gene Editing of Pklr in Human Hematopoietic Progenitors and Stem Cells for the Gene Therapy of Pyruvate Kinase Deficiency Quintana Bustamante, O., Fananas-Baquero, S., Dever, D. P., Omaira, A., Camarena, J., Sanchez-Dominguez, R., Morin, M., Fernandez, V., Angel Moreno-Pelayo, M., Bueren, J. A., Porteus, M., Segovia, J. C. AMER SOC HEMATOLOGY. 2018

View details for DOI 10.1182/blood-2018-99-111772

View details for Web of Science ID 000454842807199