PHASE 1/2A CLINICAL TRIAL OF GENE-CORRECTED AUTOLOGOUS CELL THERAPY FOR RECESSIVE DYSTROPHIC EPIDERMOLYSIS BULLOSA Gorell, E., Eichstadt, S., Barriga, M., Ponakala, A., Teng, C., Nguyen, N., Siprashvili, Z., Nazaroff, J., Chiou, A., Taylor, L., Khuu, P., Keene, D., Rieger, K., Khosla, R., Lorenz, H. P., Furukawa, L., Marinkovich, M. P., Tang, J. Y. ACTA DERMATO-VENEREOLOGICA. 2020: 75

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